What recent development has occurred in the treatment of haemophilia in India
Indian scientists have developed a novel gene therapy treatment for haemophilia.
- Indian scientists have developed a novel gene therapy treatment for haemophilia, a genetic blood disorder that prevents blood clotting.
- This treatment involves inserting a functional copy of the F8 gene, responsible for blood clotting, into patients' cells using a viral vector.
- By replacing the defective gene with the functional one, this gene therapy aims to restore the production of clotting factor VIII in haemophilia patients.
- This breakthrough offers the potential for a long-term cure for haemophilia, reducing the dependence on regular clotting factor infusions.
- The scientists have conducted successful preclinical trials, demonstrating the safety and efficacy of this gene therapy approach.
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